Status | Study |
Not yet recruiting |
Study Name: Therapeutic Use of Tadekinig Alfa in NLRC4 Mutation and XIAP Deficiency Condition: NLRC4-MAS XIAP Deficiency Date: 2017-02-28 Interventions: Drug: Tadekinig alfa Tadekinig |
Enrolling by invitation |
Study Name: MINGO Supplemental Trial in X-linked Dystonia-Parkinsonism Patients Condition: X-Linked Dystonia Parkinsonism Date: 2017-01-09 Interventions: Dietary Supplement: MINGO 6 20oz sachets will be taken daily by intervention group |
Recruiting |
Study Name: Assessment of Immunogenicity of Zostavax® in Patients With Antibody Deficiency 60 Years of Age and Older Condition: Common Variable Immune Deficiency Specific Antibody Deficiency Date: 2016-10-03 Interventions: Biological: Zostavax® Zostavax® immunization |
Active, not recruiting |
Study Name: Efficacy of Stem Cell Therapy in Ambulatory and Non-ambulatory Children With Duchenne Muscular Dystrophy - Phase 1-2 Condition: Duchenne Muscular Dystrophy Date: 2015-06-16 Interventions: Drug: Biological: Umbilical Cord Based Allogenic Mesenchymal Stem Cell |
Enrolling by invitation |
Study Name: Phase 3 Extension Study of Ataluren (PTC124) in Patients With Nonsense Mutation Dystrophinopathy Condition: Muscular Dystrophy, Duchenne Muscular Dystrophies Muscular Date: 2014-03-17 Interventions: Drug: Ataluren Other Name: PTC124 |
Completed |
Study Name: Bipolar Research Study Using MR Imaging Condition: Bipolar Affective Disorder Date: 2014-03-07 Interventions: Other: MRI scanning |
Active, not recruiting |
Study Name: Pharmacokinetics (PK) and Safety of Subgam-VF in Primary Immunodeficiency Diseases Condition: Primary Immune Deficiency Disorders Common Variable Immunodeficiency Date: 2013-06-14 Interventions: Biological: Subgam Subgam-VF dose will be given as 1.37 of the established IGIV dose (expressed in mg/kg |
Completed |
Study Name: Phase 3 Study of Ataluren in Patients With Nonsense Mutation Duchenne Muscular Dystrophy Condition: Muscular Dystrophy, Duchenne Muscular Dystrophies Muscular Date: 2013-03-26 Interventions: Drug: Ataluren Ataluren PO 10- |
Completed |
Study Name: Bipolar Intervention Study: Cognitive Interpersonal Therapy Condition: Mania Hypomania Bipolar Affective Disorder Date: 2011-03-07 Interventions: Other: Cognitive Interpersonal Therapy |
Recruiting |
Study Name: Pharmacogenomics of Mood Stabilizer Response in Bipolar Disorder (PGBD) Condition: Bipolar Affective Disorder Date: 2011-01-06 Interventions: Drug: Mood stabilizer treatment lithium or valproate |