Status | Study |
Recruiting |
Study Name: A Safety and Tolerability Study of an Investigational Drug, ALN-TTRSC02, in Healthy Subjects Condition: Transthyretin-mediated Amyloidosis (ATTR Amyloidosis) Date: 2016-05-18 Interventions: Drug: ALN-TTRSC02 Ascending do |
Active, not recruiting |
Study Name: Tolerability and Efficacy of a Combination of Doxycycline and TUDCA in Patients With Transthyretin Amyloid Cardiomyopathy Condition: Amyloidosis; Heart (Manifestation) Senile Cardiac Amyloidosis Date: 2013-03-12 Interventions: Drug: Tauroursodeoxycholic Acid and Doxycycline |
Completed |
Study Name: Safety and Effect of Doxycycline in Patients With Amyloidosis Condition: Amyloidosis Date: 2012-08-21 Interventions: Drug: Doxycycline 100 mg po bid x 12 months 100mg by mouth twice daily for 1 year. |
Completed |
Study Name: Burden of Disease Study In Patients With Transthyretin Familial Amyloidosis Polyneuropathy (TTR-FAP) orTransthyretin Cardiomyopathy (TTR-CM) And Caregivers Condition: Transthyretin Familial Amyloidosis Polyneuropathy (TTR-FAP) Tra Date: 2012-05-21 Interventions: Other: No drug No drug. |
Completed |
Study Name: Safety and Efficacy Study of Fx-1006A in Patients With Familial Amyloidosis Condition: Familial Amyloid Polyneuropathy Date: 2006-12-06 Interventions: Drug: Fx-1006A Fx-1006A 20mg o |
Completed |
Study Name: The Effect of Diflunisal on Familial Amyloidosis Condition: Familial Amyloid Polyneuropathy Familial Amyloidosis Date: 2006-02-21 Interventions: Drug: diflunisal given twice d |