Status | Study |
Recruiting |
Study Name: Study of ACE-083 in Patients With Charcot-Marie-Tooth Disease Condition: Charcot-Marie-Tooth Disease Date: 2017-04-12 Interventions: Drug: ACE-083 Part 1 - Recombinant fusion protein. Part 2 - Recombinant fusion protein or buffer solutio |
Recruiting |
Study Name: Assessing Long Term Safety and Tolerability of PXT3003 in Patients With Charcot-Marie-Tooth Disease Type 1A Condition: Charcot-Marie-Tooth Disease, Type IA Date: 2016-12-26 Interventions: Drug: PXT3003 Liquid oral solution, 5 mL bid for 9 consecutive months |
Recruiting |
Study Name: Charcot-Marie-Tooth Disease (CMT) Infant Scale (INC-6611) Condition: Charcot-Marie-Tooth Disease Date: 2016-11-29 Interventions: Other: No intervention involved |
Not yet recruiting |
Study Name: BALTiC Study: A Feasibility Analysis of Home Based BALance Training in People With Charcot-Marie-Tooth Disease Condition: Charcot-Marie-Tooth Disease, Type IA Date: 2016-11-28 Interventions: Behavioral: Falls management plus exercise training |
Recruiting |
Study Name: Ulipristal Acetate In Disease Charcot-Marie-Tooth Type of 1A Condition: CMT1A Date: 2015-11-04 Interventions: Drug: EllaOne |
Not yet recruiting |
Study Name: Tools for Therapeutic Evaluation in Charcot-Marie-Tooth Disease Type 1A: Outcome Measures and Biomarkers Condition: Charcot-Marie-Tooth Disease Type 1A Date: 2015-10-30 Interventions: Other: Clinical evaluation Other: electrop |
Active, not recruiting |
Study Name: Phase III Trial Assessing the Efficacy and Safety of PXT3003 in CMT1A Patients (PLEO-CMT) Condition: Charcot-Marie-Tooth Disease Type 1A Date: 2015-09-28 Interventions: Drug: PXT3003 dose 1 Liquid or |
Completed |
Study Name: Mexiletine for Muscle Cramps in Charcot Marie Tooth Disease Condition: Charcot Marie Tooth Disease Date: 2015-09-24 Interventions: Other: Placebo 240 mg lactose |
Completed |
Study Name: An Analysis of the Symptomatic Domains Most Relevant to Charcot Marie Tooth Neuropathy (CMT) Patients Condition: Charcot Marie Tooth Disease (CMT) Heredit Date: 2015-04-20 |
Completed |
Study Name: Disability Severity Scale (DSI) and Hereditary Motor and Sensory Neuropathy Overall Disability Scale (HMSN-R-ODS) Condition: Charcot Marie Tooth Disease Inherited Peripheral Neuropathy Date: 2014-04-02 |