Status | Study |
Recruiting |
Study Name: Trial on Safety and Efficacy of Velmanase Alfa Treatment in Pediatric Patients With Alpha-Mannosidosis Condition: Alpha-Mannosidosis Date: 2016-11-25 Interventions: Drug: Velmanase Alfa (e.g. Lamazym) iv infusion treatment |
Completed |
Study Name: Evaluation of Long-term Efficacy of Treatment With Lamazym Condition: Alpha-Mannosidosis Date: 2015-02-09 Interventions: Drug: Lamazym recombinant human alpha-mannosidase Ot |
Recruiting |
Study Name: MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis Condition: Mucopolysaccharidosis Disorders Hurler Syndrome Hunter Syn Date: 2014-06-20 Interventions: Biological: Stem Cell Transplantation |
Recruiting |
Study Name: Clinical Biomarkers in Alpha-mannosidosis Condition: Alpha-Mannosidosis Date: 2014-05-15 |
Recruiting |
Study Name: Reduced Intensity Conditioning in Patients Aged ≤35 With Non-Malignant Disorders Undergoing UCBT, BMT, or PBSCT Condition: Primary Immunodeficiency Syndromes Congenital Bone Marrow Failure Syndromes Date: 2013-10-10 Interventions: Drug: Hydroxyurea Hydroxyurea |
Active, not recruiting |
Study Name: Lamazym Aftercare Study FR Designed to Provide Treatment for French Patients Condition: Alpha-Mannosidosis Date: 2013-07-16 Interventions: Drug: Lamazym ERT, i.v. infusions weekly Other Names |
Active, not recruiting |
Study Name: Lamazym Aftercare Study Condition: Alpha-Mannosidosis Date: 2013-06-12 Interventions: Drug: Lamazym ERT, i.v. infusions weekly Other Names |
Completed |
Study Name: Longitudinal Studies of the Glycoproteinoses Condition: Aspartylglucosaminuria Fucosidosis Galactosialidosis Date: 2013-05-22 |
Completed |
Study Name: Long-term Efficacy and Safety of Lamazym for the Treatment of Patients With Alpha-Mannosidosis Condition: Alpha-Mannosidosis Date: 2012-08-22 Interventions: Drug: Lamazym ERT, i.v. infusions weekly Other Names |
Completed |
Study Name: A Placebo-Controlled Phase 3 Trial of Repeated Lamazym Treatment of Subjects With Alpha-Mannosidosis Condition: Alpha-Mannosidosis Date: 2012-08-22 Interventions: Drug: Lamazym ERT, i.v. infusi |