Status | Study |
Active, not recruiting |
Study Name: Pharmacokinetic, and Dose Response Study of Asfotase Alfa in Adult Patients With Pediatric-Onset Hypophosphatasia (HPP) Condition: Hypophosphatasia Date: 2016-05-23 Interventions: Drug: Asfotase alfa Other Name: Strensiq |
Not yet recruiting |
Study Name: Characterisation of Adult-Onset Hypophosphatasia Condition: Hypophosphatasia Date: 2016-05-04 Interventions: Other: no intervention - observational study |
Not yet recruiting |
Study Name: Health Burden of Hypophosphatasia Condition: Hypophosphatasia Date: 2016-04-01 Interventions: Other: no intervention |
Recruiting |
Study Name: Study of ALXN1101 in Neonates With Molybdenum Cofactor Deficiency (MOCD) Type A Condition: Molybdenum Cofactor Deficiency, Type A Date: 2015-12-03 Interventions: Drug: ALXN1101 |
Recruiting |
Study Name: Biomarker for Hypophosphatasia Disease Condition: HEREDITARY DISEASES METABOLISM, INBORN ERRORS Hypophosphat Date: 2015-11-10 |
Completed |
Study Name: Post-approval Clinical Study of Asfotase Alfa Treatment for Patients With Hypophosphatasia (HPP) in Japan Condition: Hypophosphatasia Date: 2015-08-11 Interventions: Biological: Asfotase Alfa Other Name: Strensiq |
Approved for marketing |
Study Name: Expanded Access Program for Asfotase Alfa Treatment for Patients With Infantile- or Juvenile-onset Hypophosphatasia (HPP) Condition: Hypophosphatasia Date: 2015-07-08 Interventions: Biological: asfotase alfa Patients participating in this program will receive 6 mg/kg/week asfotase alfa |
Completed |
Study Name: Safety and Efficacy of Asfotase Alfa in Patients With Hypophosphatasia (HPP) Condition: Hypophosphatasia Date: 2015-03-26 Interventions: Drug: Asfotase Alfa (ALXN1215) Other Name: ALXN1215 |
Enrolling by invitation |
Study Name: An Observational, Longitudinal, Prospective, Long-Term Registry Of Patients With Hypophosphatasia (HPP) Condition: Hypophosphatasia (HPP) Date: 2014-11-26 |
Completed |
Study Name: Burden of Disease in Hypophosphatasia (HPP) Condition: Hypophosphatasia Date: 2014-11-11 |