Status | Study |
Recruiting |
Study Name: Prospective Evaluation of Infants With Spinal Muscular Atrophy: Condition: Spinal Muscular Atrophy Date: 2016-07-01 |
Enrolling by invitation |
Study Name: A Study for Participants With Spinal Muscular Atrophy (SMA) Who Previously Participated in Nusinersen (ISIS 396443) Investigational Studies. Condition: Spinal Muscular Atrophy Date: 2015-10-30 Interventions: Drug: nusinersen Administered by intrathecal (IT) injection |
Active, not recruiting |
Study Name: A Study to Assess the Safety and Tolerability of Nusinersen (ISIS 396443) in Participants With Spinal Muscular Atrophy (SMA). Condition: Spinal Muscular Atrophy Date: 2015-05-14 Interventions: Drug: Nusinersen Administered |
Completed |
Study Name: A Study to Assess the Efficacy and Safety of Nusinersen (ISIS 396443) in Participants With Later-onset Spinal Muscular Atrophy (SMA) Condition: Spinal Muscular Atrophy Date: 2014-11-12 Interventions: Drug: nusinersen Administered |
Active, not recruiting |
Study Name: An Open Label Study of LMI070 in Type 1 Spinal Muscular Atrophy (SMA) Condition: Spinal Muscular Atrophy Date: 2014-10-01 Interventions: Drug: LMI070 |
Completed |
Study Name: A Study to Assess the Efficacy and Safety of Nusinersen (ISIS 396443) in Infants With Spinal Muscular Atrophy Condition: Spinal Muscular Atrophy Date: 2014-07-14 Interventions: Drug: nusinersen Administered |
Completed |
Study Name: Newborn Screening for Spinal Muscular Atrophy Condition: Spinal Muscular Atrophy Date: 2014-04-21 Interventions: Other: newborn screening test for SMA Routine newborn screening dried blood spots sample is used to test |
Active, not recruiting |
Study Name: A Study to Assess the Efficacy, Safety and Pharmacokinetics of Nusinersen (ISIS 396443) in Infants With Spinal Muscular Atrophy (SMA) Condition: Spinal Muscular Atrophy Date: 2013-04-22 Interventions: Drug: nusinersen Administered by intrathecal (IT) injection |
Completed |
Study Name: An Open-label Safety and Tolerability Study of Nusinersen (ISIS 396443) in Participants With Spinal Muscular Atrophy Who Previously Participated in ISIS 396443-CS1 (NCT01494701) Condition: Spinal Muscular Atrophy Date: 2013-01-28 Interventions: Drug: nusinersen Administered by intrathecal (IT) injection |
Enrolling by invitation |
Study Name: Mechanisms of Cell Death in Spinal Muscular Atrophy Condition: Spinal Muscular Atrophy Date: 2012-12-13 |