Clinical Trial: FA Clinical Outcome Measures

Study Status: Recruiting
Recruit Status: Recruiting
Study Type: Observational [Patient Registry]




Official Title: Clinical Outcome Measures in Friedreich's Ataxia

Brief Summary: This multicenter natural history study aims to expand the network of clinical research centers in FA, and to provide a framework for facilitating therapeutic interventions. In addition, this study will lead to the development of valid yet sensitive clinical measures crucial to outcome assessment of patients with Friedreich's Ataxia. This study will support genetic modifier studies, biomarker studies, and frataxin protein level assessments by building a sample repository.