Clinical Trial: Children With Lysosomal Acid Lipase Deficiency Who Previously Received Treatment With SBC-102

Study Status: Terminated
Recruit Status: Terminated
Study Type: Interventional




Official Title: An Open Label Multicenter Extension Study to Evaluate the Long-term Efficacy and Safety of SBC-102 in Children With Lysosomal Acid Lipase Deficiency Who Previously Received Treatment With SBC-102

Brief Summary: This phase 2/3, open-label extension study will evaluate the long-term efficacy and safety of intravenous (IV) infusions of SBC-102 in children with Lysosomal Acid Lipase (LAL) Deficiency who previously received treatment with SBC-102.