Clinical Trial: Long-term Deferiprone Treatment in Patients With Pantothenate Kinase-Associated Neurodegeneration

Study Status: Active, not recruiting
Recruit Status: Active, not recruiting
Study Type: Interventional




Official Title: Long-term Safety and Efficacy Study of Deferiprone in Patients With Pantothenate Kinase-Associated Neurodegeneration (PKAN)

Brief Summary: Patients with PKAN will be treated with the iron chelator deferiprone for 18 months. Only patients who have completed the earlier study TIRCON2012V1 (a double-blind placebo-controlled trial in which participants were randomized to receive either deferiprone or placebo for 18 months) are eligible to enroll.