Clinical Trial: Compassionate Use of Deferiprone in Patients With PKAN

Study Status: Available
Recruit Status: Available
Study Type: Expanded Access




Official Title: The Compassionate Use of Deferiprone in Patients With Pantothenate Kinase-Associated Neurodegeneration

Brief Summary: Patients with pantothenate kinase-associated neurodegeneration (PKAN) who have completed the ApoPharma-sponsored study TIRCON2012V1-EXT and who wish to continue to take deferiprone will be offered the opportunity to receive it on a compassionate basis. Patients will be followed locally by their own neurologist or other appropriate specialist.