Status | Study |
Recruiting |
Study Name: Cure Cystinosis International Registry Condition: Cystinosis Nephropathic Cystinosis Date: 2011-03-29 |
Active, not recruiting |
Study Name: Long-Term Safety Follow-up Study of Cysteamine Bitartrate Delayed-release Capsules (RP103) Condition: Cystinosis Date: 2010-09-03 Interventions: Drug: Cysteamine Bitartrate Delayed-release Capsules (RP103) RP103 every 12H, supplied in 75 and 25mg ca |
Completed |
Study Name: Phase 3 Study of Cysteamine Bitartrate Delayed-release (RP103) Compared to Cystagon® in Patients With Cystinosis Condition: Cystinosis Date: 2009-10-22 Interventions: Drug: Cystagon® (Cysteamine Bitartrate) |
Completed |
Study Name: Pilot Study of Safety, Tolerability, Pharmacokinetics/Pharmacodynamics of RP103 Compared to Cystagon® in Patients With Cystinosis Condition: Cystinosis Date: 2009-03-27 Interventions: Drug: Cystagon® |
Completed |
Study Name: Clinical and Biological Study of Sub-pigmentation During Infantile Cystinosis Condition: Cystinosis Date: 2009-01-13 Interventions: Other: analysis of pigmentation cutting hair, skin description, skin biopsy for only 4 patients |
Recruiting |
Study Name: Use of Cysteamine in the Treatment of Cystinosis Condition: Cystinosis Date: 2006-08-01 Interventions: Drug: Cysteamine Cystine-depleting agent |
Completed |
Study Name: Salivary Proteins in Disease and Health Condition: Diabetes Mellitus Sarcoidosis Dental Caries Date: 2004-12-23 |
Completed |
Study Name: Kidney Transplantation in Patients With Cystinosis Condition: Cystinosis Date: 2003-12-12 |
Completed |
Study Name: The Role of Susceptibility to Thrombosis in the Pseudotumor Cerebri of Nephropathic Cystinosis: A Case-Control Study Condition: Pseudotumor Cerebri Cystinosis Date: 2003-11-03 |
Completed |
Study Name: Randomized Study of New Formulation Ophthalmic Cysteamine Hydrochloride for Corneal Cystine Accumulation in Patients With Cystinosis Condition: Cystinosis Date: 2001-02-02 Interventions: Drug: cysteamine hydrochloride |