Status | Study |
NOT_YET_RECRUITING |
Study Name: Observational Follow-up Study of Haplo-identical Transplants in Fanconi Disease Condition: Date: 2023-06-06 Interventions: Additional blood samples at J100, M6, M12, M24 |
Recruiting |
Study Name: Clinical Phase II Trial to Evaluate CD34+ Cells Mobilization and Collection in Patients With Fanconi Anemia for Subsequent Transduction With a Lentiviral Vector Carring FANCA Gene. FANCOSTEM-1 Condition: Fanconi Anemia Date: 2016-09-06 Interventions: Drug: filgrastim G-CSF (12 |
Recruiting |
Study Name: Mobilization and Collection of Peripheral Blood Stem Cells in Patients With Fanconi Anemia Using G-CSF and Plerixafor Condition: Fanconi Anemia Date: 2016-02-05 Interventions: Drug: G-CSF D1 to D4 : Injecti |
Enrolling by invitation |
Study Name: Unrelated HSCT in Patients With Fanconi Anemia Condition: Fanconi Anemia Date: 2012-10-19 Interventions: Biological: CD34+ selected cells Compassionate treatment of Fanconi Anemia patients with unrelated bone |
Recruiting |
Study Name: Quercetin in Children With Fanconi Anemia; a Pilot Study Condition: Fanconi Anemia Date: 2012-07-25 Interventions: Drug: Quercetin (dietary supplement) Quercetin will be given orally on a twice a day schedule starting w |
Recruiting |
Study Name: Gene Therapy for Fanconi Anemia Condition: Fanconi Anemia Date: 2011-03-16 Interventions: Procedure: Bone Marrow Aspiration |
Completed |
Study Name: Multicenter Transplant Study for Fanconi Anemia Condition: Fanconi Anemia Date: 2010-03-05 Interventions: Drug: Chemotherapy Busulfan 0. |
Completed |
Study Name: Pilot Study of Etanercept (Enbrel) in Children With Fanconi Anemia Condition: Fanconi Anemia Date: 2009-08-24 Interventions: Drug: Etanercept All qualified subjects receive 24 weekly subcutaneous injections of Etanercept. |
Active, not recruiting |
Study Name: Hematopoietic Stem Cell Transplant for Fanconi Anemia Condition: Fanconi Anemia Date: 2009-05-20 Interventions: Device: CliniMACs device Donor Peripheral blood progenitor cells will use CD34+ selection with the use o |
Terminated |
Study Name: Gene Function in Bone Marrow Cells From Patients With Fanconi Anemia and From Healthy Participants Condition: Fanconi Anemia Date: 2009-05-09 Interventions: Genetic: microarray analysis Procedure: bi |