Status | Study |
Terminated |
Study Name: Treatment of TNNT1-Myopathy With L-Tyrosine. Condition: Nemaline Myopathy Date: 2013-07-02 Interventions: Drug: L-Tyrosine Drug: Placebo |
Recruiting |
Study Name: Congenital Muscle Disease Study of Patient and Family Reported Medical Information Condition: Congenital Muscular Dystrophy (Including Unspecified/Undiagnosed) Dystroglycanopathy Date: 2011-07-26 |
Recruiting |
Study Name: Molecular and Genetic Studies of Congenital Myopathies Condition: Central Core Disease Centronuclear Myopathy Congenital Fib Date: 2006-01-05 |